Stem cells show promise in Phase I/IIa trial - CNS10-NPC-GDNF

[lynnbr2]

“Because [these stem cells] are engineered to release GDNF, we get a ‘double whammy’ approach where both the new cells and the [GDNF] protein could help dying motor neurons survive better in this disease,”...

Stem Cell-based Therapy to Produce GDNF Found Safe in ALS Trial |...

Stem cells engineered to produce GDNF, a key factor for motor neuron survival, were safely delivered into ALS patients, an early trial showed.

alsnewstoday.com

 

[lgelb]

It is exciting work, but important to note this study has only established safety, not efficacy.