Reldesemtiv earns FDA Orphan status...now what?

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blitzc

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Moderators: Is it acceptable to post these articles? I know there are rules, so remove if necessary.

So can the wiser ones among us please explain "Now what?" What happens next at this stage of orphan status? What else do those of you with other knowlege know about this drug?

At what point do I (or others of us) contact our neurologist and inquire about it? Or other drugs making progress?
 

Nikki J

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The articles look ok. Links that have donation buttons or are sales are not ok

orphan drug status is not approval. It gives the company a financial break if they eventually apply for approval. With this they would need more clinical trials before it could go anywhere. Sorry but I wouldn’t get too excited
 

blitzc

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Thanks for that explanation!
 

KarenNWendyn

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It sounds promising, but it also sounds similar to Tirasimptev which ultimately didn’t pan out. Tirasimptev continues VIGOR ALS

If it does well in phase 3 trials, I can see it being part of the cocktail. But denervation still needs to be stopped (this drug doesn’t do that).
 
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