Orphazyme Clinical Trial Hits Full Enrollment

Ken15

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This Phase 3 enrollment notice was posted today.

Earlier this year, results of the prior Phase 2/3 trial were published.
 

morleyde

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Is this drug used to treat MND's? This drug study is for NPC.
 

Nikki J

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This trial is for ALS as it says in the link. There was a previous trial in sod1 ALS that showed some increased survival
 

morleyde

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I see that.
The Phase 2/3 link was for NPC.
 

Ken15

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Is this drug used to treat MND's? This drug study is for NPC.
My apologies. I incorrectly posted the Phase 2/3 link for NPC.

Nikki posted the correct link to the Phase 2/3 SOD1 ALS result.

Ken
 

Ulf

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I'm part of it. It tones down the fasciculations a lot.
 

Phil47

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I'm on the trial, too. No noticeable effects. Could be on placebo. Ulf, how long have you been on the trial? Anyone else out there on the trial?
 

Ulf

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Phil47

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I joined trial later than you. Any other benefits / effects? Best wishes to you.
 

Ulf

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It slows down the disease progression.
 
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