KevinM
Senior member
- Joined
- Mar 30, 2019
- Messages
- 559
- Reason
- PALS
- Diagnosis
- 06/2019
- Country
- US
- State
- FL
- City
- Tallahassee
I know that today’s release of the phase 3 data is an incredible letdown for so many PALS hoping this would be the treatment that might halt or restore function. So many had pinned their hopes on dramatically positive results, which did not occur. It does seem to have a positive effect on early stage patients, and the biomarkers identified are helpful, but it fell far short of everyone’s hopes and dreams.
As Brian Wallach said, it works, but the question is for whom and at what rate of infusions. I think it also demonstrates the power of the placebo effect given the very high rate of response in those patients.
My neurologist had expressed his doubts about dramatic results several months ago after parsing all the previous data, and it appears he was right. What a shame. Kevin
As Brian Wallach said, it works, but the question is for whom and at what rate of infusions. I think it also demonstrates the power of the placebo effect given the very high rate of response in those patients.
My neurologist had expressed his doubts about dramatic results several months ago after parsing all the previous data, and it appears he was right. What a shame. Kevin