Arimoclomol trial now recruiting

[lgelb]

List of sites here

Must be within 18 months of diagnosis, have an FRS of at least 35 and erect SVC% predicted equal to or above 80% at screening, and not use BiPAP more than 2 hours while awake. The trial recruitment page is not as clear as the NIH entry on those criteria.

 

[Par220]

Just heard they seem to be offering early access of arimoclomol for those interested and not eligible for the trial. Scroll down on this link for details.

https://www.orphazyme.com/clinical-programme/