Nikki J
Moderator
- Joined
- Mar 22, 2012
- Messages
- 16,459
- Reason
- PALS
- Diagnosis
- 04/2014
- Country
- US
- State
- MA
- City
- Boston
As many of you know antisense genetic therapy is hopeful for FALS. The SOD1 trial is in phase 3. C9 is in a phase1-2. FUS is coming to trial in the next year
however Ionis has an antisense targeting ATXN-2 TDP-43 Is involved which is found in SALS ( and many FALS). They SAY they expect a trial to start in the latter part of this year. My experience is that it may well take longer but this is incredibly hopeful news for SALS
however Ionis has an antisense targeting ATXN-2 TDP-43 Is involved which is found in SALS ( and many FALS). They SAY they expect a trial to start in the latter part of this year. My experience is that it may well take longer but this is incredibly hopeful news for SALS