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    Biogen c9 aso stopped

    What do you mean Waves had a special design? Do you mean that Waves looks to only attack the bad copy of the gene vs both in Biogens? What is Dr. Browns approach?
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    Biogen c9 aso stopped

    Any word on if Wave's aso clinical trial is still going? Have they commented at all?
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    Biogen c9 aso stopped

    Biogen's ASO targets the V1 and V3 variants on the mutated and normal chromosome. Wave only targets those on the mutated chromosome. Hopefully that is the issue.
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    Biogen c9 aso stopped

    The report says it did not support the hypothesis that reducing RNA and DPRs would stop disease progression. It does not say if these were reduced in patients and by how much. Hopefully they weren't reduced enough? There arent many details. How long does it take to get the full results usually?
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    Biogen c9 aso stopped

    Unfortunately I do not have access to message to Dr. Harms anymore about his thoughts. He did say awhile ago that the other ASO's (Wave and Dr. Brown out of UMASS) are different enough so hopefully their results and other C9 treatments could be positive. Will Biogen try another C9 treatment...
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    Request for advice regarding best treatment for C9

    Do they schedule you for an appointment right away or is there usually a waiting list?
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    Request for advice regarding best treatment for C9

    Cant you stop the experimental treatment like one month before the first trial appointment? There usually are limits how long you need to be off of something to participate in a trial
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    questions gravity feeding

    We crushed pills, mixed with water, and poured down the syringe the same as we did for the formula. We got the silent knight pill crusher off of amazon. It is a little pricey but it worked very well. We started with a cheaper option but it could not crush the pills small enough to go down the...
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    questions gravity feeding

    do not draw fluid into it. we did not use the piston. hook up the syringe to the tube and pour formula into it.
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    questions gravity feeding

    We let it flow through on its own through the syringe. We did mix it with about 8 ounces of water first. This helped my dad get his daily water intake and also thinned out the formula so it would flow faster.
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