Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies
Conditions: Sickle Cell Disease; Transfusion Dependent Alpha- or Beta- Thalassemia; Diamond Blackfan Anemia; Paroxysmal Nocturnal Hemoglobinuria; Glanzmann Thrombasthenia; Severe Congenital Neutropenia; Shwachman-Diamond Syndrome; Non-Malignant Hematologic Disorders
Interventions: Drug: Reduced Toxicity Ablative Regimen; Drug: Reduced Intensity Preparative Regimen; Drug: Myeloablative Preparative Regimen
Sponsor: Masonic Cancer Center, University of Minnesota
Recruiting - verified February 2017
Interventions: Drug: Reduced Toxicity Ablative Regimen; Drug: Reduced Intensity Preparative Regimen; Drug: Myeloablative Preparative Regimen
Sponsor: Masonic Cancer Center, University of Minnesota
Recruiting - verified February 2017